Raremark | Rare disease community

Zephyrus II clinical research study

ADventure trial for Adult CAH by Adrenas therapeutics

Clinical study in myasthenia gravis

Myasthenia gravis clinical study

Idiopathic pulmonary fibrosis clinical study

Urea Cycle Disorder clinical study

Phillip's Story: Growing up with sickle Cell

What does it mean to be an advocate?

Setting goals for yourself and the greater sickle cell community

Phillip's story: Knowing what you can control, and what you can't

Phillip's story: Growing up with sickle cell

What it means to be a Sickle Cell Warrior

Sickle cell and the basics of gene therapy

Shamonica's story: Why self care is so important

Common concerns about gene therapy for sickle cell

Gene therapy for sickle cell: When can we expect it?

Shamonica's Story: Self care means making yourself the priority

How can you become an advocate?

Ijeoma's story: Living life to the fullest

Ijeoma's story: How you can become an advocate

Ijeoma's story: "You don't look like you have sickle cell"

Ijeoma's story: Starting my advocacy journey

Ijeoma's story: Inspiring others by living life to the fullest

How can I access genetic counseling services?

"I have a blood relative with IPF: How can genetic testing help me understand my risk?"

Genetic testing and IPF: Clinical testing vs. research testing

Genetic testing and IPF: What can the results tell us?

Is IPF genetic?

Don't wait before seeking an IPF expert