1:19:38
Update on Ultragenyx's Sanfilippo syndrome Type A Gene Therapy program (UX111) - March 26, 2024
377 views • 1 month ago
2:58
Saving Veda from Sanfilippo syndrome
1.8K views • 2 months ago
3:10
A Message to You on the 10-Year Anniversary of Cure Sanfilippo Foundation
961 views • 4 months ago
11:07
Development of Global Consensus Clinical Care Guidelines for Sanfilippo Syndrome, WORLDSymposium2023
136 views • 10 months ago
3:31
Parents' first watch of a video they hope will save their daughter Liv
1.7K views • 1 year ago
3:15
This video can save our 3-year-old daughter's life: #SavingLiv
9.1K views • 1 year ago
0:15
Saving Liv - Coming Saturday, Dec. 3
192 views • 1 year ago
8:20
New Sanfilippo drug repurposing clinical trial; updates on other research + more
606 views • 1 year ago
3:29:34
ADVANCE 22 Sanfilippo Conference - Day 1, Part 1
328 views • 1 year ago
2:14:32
ADVANCE 22 Sanfilippo conference - Day 2, Part 3
147 views • 1 year ago
2:05:55
ADVANCE 22 Sanfilippo conference - Day 2, Part 2
81 views • 1 year ago
2:31:14
ADVANCE 22 Sanfilippo conference - Day 2, Part 1
125 views • 1 year ago
2:35:41
ADVANCE 22 Sanfilippo conference - Day 1, Part 2
214 views • 1 year ago
1:58:48
ADVANCE 22 Sanfilippo conference - Day 1, Part 3
106 views • 1 year ago
1:01
TikTok For A Cure - Kickoff from @Love_Logan07
1.9K views • 1 year ago
3:38
Alina's Story - One more miracle?
628 views • 1 year ago
8:54
WORLD Symposium highlights Anakinra early results; upcoming gene therapy trial; + more
434 views • 2 years ago
9:39
Kicking off 2022; upcoming key meeting with FDA; recent grants, WORLD conference, & more
253 views • 2 years ago
10:37
Anakinra Trial update, Collaboration with UNC, other research updates, Help Simon, & more
504 views • 2 years ago
6:42
How All Stripes can help Sanfilippo syndrome research
214 views • 2 years ago
3:04
Help Simon fight to live and play basketball
6.9K views • 2 years ago
12:49
BIG WEEK! World Sanfilippo Day & viral campaign, Trivia Gala, All Stripes & more
135 views • 2 years ago
13:10
Sanfilippo & accelerated approval; newly-diagnosed guide; World Sanfilippo Awareness Day & more
146 views • 2 years ago
1:05
2021 Step Up to Cure Sanfilippo | Wrap-Up Video
312 views • 2 years ago
11:06
Why a podcast?; Photobiomodulation research; the costs of pioneering research; + more
95 views • 2 years ago
10:34
Patient Needs & Culture of the Laboratory; Kickoff 2021 StepUp fundraiser; families milestone & more
79 views • 2 years ago
11:39
Get-to-know your child worksheet for school; Sanfilippo on TikTok; Inclusion + more
1K views • 2 years ago
12:02
Free Educator Guide; Dopamine & Reducing Autism Behaviors + more
592 views • 2 years ago
10:00
In Memory of Reagan; New testing created; $1M granted for 5 new projects + more
456 views • 2 years ago
10:49
Chan Zuckerberg, Sanfilippo biomarkers & FDA; Anakinra trial update; + more
299 views • 2 years ago
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